Eteplirsen (Exondys 51) for Duchenne: Price, Availability and Access in Pakistan
Written by the Muscular Dystrophy Pakistan (MDP) content team. Based on regulatory, company and news sources listed below. Prices and availability were checked on October 16, 2026 and can change. Few medicines have been discussed as much in the Duchenne community as eteplirsen , sold as Exondys 51 . Families see it described as the first approved medicine for Duchenne, then see a price of hundreds of thousands of dollars a year, and then ask a painful question: "Can my child get it in Pakistan?" This article gives a clear, honest answer to the questions we hear most: what eteplirsen is, who can use it, what the evidence shows, how much it costs, where it is available, whether it can be brought to Pakistan, how the cost might be reduced, and what the government can do. Quick facts Eteplirsen is a weekly intravenous (IV) infusion for boys whose genetic report shows a change in the DMD gene that is amenable to exon 51 skipping , about 13% to 14% of people with Duchenne. ...